Paroxysmal Nocturnal Hemoglobinuria Clinical Trials

Not all trials are listed on www.ClinicalTrials.gov. The investigators may have chosen not to register the trial, or the study may not be eligible to be listed on ClinicalTrials.gov. If the study has not, for example, been approved by a human subject review board, it cannot be posted. Some trials are not listed because the investigators are not planning to publish the research findings, so you can ask the study coordinator why the study has not been included on ClinicalTrials.gov before you give your consent to participate.

The information on the studies linked below is provided strictly as a resource, not as an endorsement of any given treatment, doctor, or medical center.

Remember, before you sign a consent form, Clinical Trials Explained can help you understand the potential risks and benefits of a clinical trial. You can also contact the AA&MDSIF staff to discuss any questions you have at clinicaltrials@aamds.org or by calling the office at 301.279.7202 or 800.747.2820.

^{Last Modified: February 2009}

Bone Marrow Failure Disease Consortium

Bone Marrow Failure Disease Consortium, Multiple Protocols for Aplastic Anemia, PNH, and MDS

Protocol Multiple Protocols | Multiple Sites

The National Institutes of Health (NIH) has awarded a $4.5 million research grant to the Bone Marrow Failure Disease Consortium (BMFDC). This group of expert physicians and researchers are addressing challenges in diagnosing and treating bone marrow diseases. These authorities in treating bone marrow disorders are holding clinical studies at five centers of excellence across the US, to find advances in treatment options for patients. The BMFDC functions under the umbrella of the NIH's Rare Diseases Clinical Research Network (RDCRN).

The BMFDC is studying:

aplastic anemia,
myelodysplastic syndromes,
paroxysmal nocturnal hemoglobinuria,
single lineage cytopenias such as large granular lymphocyte leukemia, and
pure red cell aplasia.

To view descriptions of all BMFDC clinical studies, visit http://rarediseasesnetwork.epi.usf.edu/bmfdc/takeaction/findatrial.htm.

For patients with: AA, MDS or PNH

Link: http://rarediseasesnetwork.epi.usf.edu/bmfdc/takeaction/findatrial.htm

Updated: December 16, 2007

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