treatment

Home Reported Outcomes in PNH: A Mobile App-Based, Prospective, Observational Program to Evaluate Disease Burden and Treatment Patterns in Paroxysmal Nocturnal Hemoglobinuria in the US

If you are interested in learning more about your possible participation in this clinical trial, please complete the form. Your information will be forwarded directly to the sponsoring company.

The study aims to longitudinally capture the full spectrum of symptoms, treatment utilization, and overall Health-Related Quality of Life (HRQoL) experienced by PNH patients. By primarily utilizing home reported outcomes (HRO) data on symptom burden and treatment usage, supplemented with patient-reported outcome (PRO) measures, the study seeks to establish a new real-world data (RWD) source to understand symptom variability and HRQoL among PNH patients, including those receiving orally administered iptacopan.

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FDA approves imetelstat for low- to intermediate-1 risk myelodysplastic syndromes with transfusion-dependent anemia

On June 6, 2024, the Food and Drug Administration approved imetelstat (Rytelo, Geron Corporation), an oligonucleotide telomerase inhibitor, for adults with low- to intermediate-1 risk

Blood Transfusions and Iron Overload

In this webinar, Dr. Thomas Coates will discuss blood transfusions and the potential side effect, iron overload. You may submit questions in advance by emailing help@aamds.org.

Understanding Secondary AML: High-Risk MDS to AML

In this webinar, Dr. Nathan Punwani discusses the development of secondary AML from high risk MDS, treatment options and the quality of life impact for patients.

A Reduced-Intensity Conditioning Regimen (Cyclophosphamide, Pentostatin, ATG) Followed by Haploidentical Hematopoietic Stem Cell Transplant for the Treatment of Patients with Refractory or Recurrent Severe Aplastic Anemia

The current standard treatment for

Kristen Schratz, MD

Schratz, Kristen

Assistant Professor of Oncology

Johns Hopkins University

Online Profile:

https://profiles.hopkinsmedicine.org/provider/Kristen+Schratz/2708235

Hiroyuki Takamori, MD

Takamori, Hiroyuki

Project Researcher

Osaka Univesity Graduate School of Medicine

Online Profile:

https://www.med.osaka-u.ac.jp/pub/bldon/outline.html#member

Yasmin Abaza, MD

Abaza, Yasmin

Assistant Professor of Medicine

Robert H. Lurie Comprehensive Cancer Center of Northwestern University

Online Profile:

https://www.cancer.northwestern.edu/research/membership/profile.html?id=8f5fecaf…

Stephen Chung, MD

Chung, Stephen

Assistant Professor of Medicine

UT Southwestern Medical Center

Stephen Chung, M.D., is an Assistant Professor in the Department of Internal Medicine and the Children’s Research Institute at UT Southwestern Medical Center. He specializes in the care of patients with the

Online Profile:

https://utswmed.org/doctors/stephen-chung/

Neal Young, MD

Young, Neal

Senior Investigator

National Heart, Lung, and Blood Institute - National Institutes of Health

Neal Young received a A.B. cum laude from Harvard College in 1967 and his M.D. in 1971 from the Johns Hopkins School of Medicine. He did post-graduate medical training at Massachusetts General Hospital and Barnes Hospital at Washington University in St. Louis before joining the NHLBI in 1981. He is a Master of the American College of Physicians and has accrued many academic honors. His efforts as a US Government employee were recognized with Samuel J. Heyman Service to America Medal in Science and the Environment. Dr.

Online Profile:

https://www.nhlbi.nih.gov/science/hematopoiesis-and-bone-marrow-failure

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