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Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
IPSS-M in myelodysplastic neoplasms arising from aplastic anemia and paroxysmal nocturnal hemoglobinuria Jun 2023 Blood Aplastic Anemia
Alternative donor BMT with post-transplant cyclophosphamide as initial therapy for acquired severe aplastic anemia Apr 2023 Blood Aplastic Anemia
How I Treat Paroxysmal nocturnal hemoglobinuria Jan 2021 Blood Paroxysmal Nocturnal Hemoglobinuria (PNH)
A genomics-informed computational biology platform prospectively predicts treatment responses in AML and MDS patients Jun 2019 Blood Advances Myelodysplastic Syndromes (MDS)
Venetoclax and Hypomethylating Agents (HMAs) Induce High Response Rates in MDS, Including Patients After HMA Therapy Failure Jul 2020 Blood Advances Myelodysplastic Syndromes (MDS)
Guideline-based indicators for adult patients with myelodysplastic syndromes Aug 2020 Blood Advances Myelodysplastic Syndromes (MDS)
Pegcetacoplan controls hemolysis in complement inhibitor-naive patients with paroxysmal nocturnal hemoglobinuria Jun 2023 Blood Advances Paroxysmal Nocturnal Hemoglobinuria (PNH)
An agenda to advance research in myelodysplastic syndromes: a TOP 10 priority list from the first international workshop in MDS Jun 2023 Blood Advances Myelodysplastic Syndromes (MDS)
Haploidentical BMT for severe aplastic anemia with intensive GVHD prophylaxis including posttransplant cyclophosphamide Apr 2020 Blood Advances Aplastic Anemia
A phase 3 randomized study of 5-azacitidine maintenance vs observation after transplant in high-risk AML and MDS patients Nov 2020 Blood Advances Myelodysplastic Syndromes (MDS)