Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
A study assessing the feasibility of randomization of pediatric and young adult patients between matched unrelated donor bone marrow transplantation and immune-suppressive therapy for newly diagnosed severe aplastic anemia: A joint pilot trial of the Nort Pediatric Blood & Cancer Aplastic Anemia, Pediatric
Diagnosis and treatment of pediatric myelodysplastic syndromes: A survey of the North American Pediatric Aplastic Anemia Consortium Pediatric Blood & Cancer Aplastic Anemia, Myelodysplastic Syndromes (MDS), Pediatric
Treatment of newly diagnosed severe aplastic anemia in children: Evidence-based recommendations Pediatric Blood & Cancer Aplastic Anemia
Eltrombopag in children with severe aplastic anemia Pediatric Blood & Cancer Aplastic Anemia, Pediatric
Treatment of relapsed/refractory severe aplastic anemia in children: Evidence-based recommendations Pediatric Blood Cancer Aplastic Anemia
Treatment of newly diagnosed severe aplastic anemia in children: Evidence-based recommendations Pediatric Blood Cancer Aplastic Anemia, Pediatric
Family reflections: pediatric aplastic anemia research; a parent perspective Pediatric Research Aplastic Anemia, Pediatric
Family reflections: George Elliott: a first-person commentary on pediatric aplastic anemia research Pediatric Research Aplastic Anemia
Patient preferences and quality of life implications of ravulizumab (every 8 weeks) and eculizumab (every 2 weeks) for the treatment of paroxysmal nocturnal hemoglobinuria. PloS One Paroxysmal Nocturnal Hemoglobinuria (PNH)
Improvements in hematologic markers and decreases in fatigue with pegcetacoplan for patients with paroxysmal nocturnal hemoglobinuria and mild or moderate anemia (hemoglobin ≥10 g/dL) who had received eculizumab or were naive to complement inhibitors PLOS One Paroxysmal Nocturnal Hemoglobinuria (PNH)

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