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Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
Understanding pharmacological complement inhibition in paroxysmal nocturnal hemoglobinuria Mar 2024 Haematologica Paroxysmal Nocturnal Hemoglobinuria (PNH)
Phase II trials of zilucoplan in paroxysmal nocturnal hemoglobinuria Mar 2024 Haematologica Paroxysmal Nocturnal Hemoglobinuria (PNH)
Paroxysmal nocturnal hemoglobinuria: Review of the patient experience and treatment landscape Mar 2024 Blood Reviews Paroxysmal Nocturnal Hemoglobinuria (PNH)
Oral Iptacopan Monotherapy in Paroxysmal Nocturnal Hemoglobinuria Mar 2024 The New England Journal of Medicine Paroxysmal Nocturnal Hemoglobinuria (PNH)
SOHO State of the Art Updates and Next Questions: An Update on Higher Risk Myelodysplastic Syndromes Mar 2024 Clinical Lymphoma, Myeloma & Leukemia Myelodysplastic Syndromes (MDS)
Expert consensus on the management of pharmacodynamic breakthrough-hemolysis in treated paroxysmal nocturnal hemoglobinuria Mar 2024 Hematology. Paroxysmal Nocturnal Hemoglobinuria (PNH)
Luspatercept in low-risk myelodysplastic syndromes: a paradigm shift in treatment strategies Mar 2024 Expert Opinion on Biological Therapy Myelodysplastic Syndromes (MDS)
Safety and Efficacy of Pegcetacoplan in Adult Patients with Paroxysmal Nocturnal Hemoglobinuria over 48 Weeks: 307 Open-Label Extension Study Apr 2024 Advances in Therapy Paroxysmal Nocturnal Hemoglobinuria (PNH)
T-cell dysfunctions in myelodysplastic syndromes Apr 2024 Blood Myelodysplastic Syndromes (MDS)
Quality of life after immune suppressive therapy in aplastic anemia Apr 2024 Annals of Hematology Aplastic Anemia