Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Sort ascending Original Publication Date Journal Bone Marrow Disease
Real-world experience of pegcetacoplan in paroxysmal nocturnal hemoglobinuria American Journal of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Real-world Effectiveness of Azacitidine in Treatment-Naive Patients With Higher-risk Myelodysplastic Syndromes Clinical Lymphoma, Myeloma & Leukemia Myelodysplastic Syndromes (MDS)
Real-World Effectiveness and Safety of Ravulizumab in Patients With Paroxysmal Nocturnal Hemoglobinuria: Evidence From the International PNH Registry American Journal of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Real-world clinical outcomes and treatment response in complement inhibitor experienced and naïve PNH patients prescribed pegcetacoplan in Europe and Canada Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
RBC transfusion independence among lower risk MDS patients receiving hypomethylating agents: a population-level analysis Leukemia & Lymphoma Myelodysplastic Syndromes (MDS)
Ravulizumab: a novel C5 inhibitor for the treatment of paroxysmal nocturnal hemoglobinuria Therapeutic Advances in Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Randomized trials with checkpoint inhibitors in acute myeloid leukaemia and myelodysplastic syndromes: What have we learned so far and where are we heading? Best practice & research. Clinical haematology Myelodysplastic Syndromes (MDS)
Raising the bar for lower-risk myelodysplastic syndromes Leukemia & Lymphoma Myelodysplastic Syndromes (MDS)
Raising the bar for lower-risk myelodysplastic syndromes Leukemia & Lymphoma Myelodysplastic Syndromes (MDS)
Quality of life after immune suppressive therapy in aplastic anemia Annals of Hematology Aplastic Anemia

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