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Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
Oral decitabine cedazuridine with and without venetoclax in higher-risk myelodysplastic syndromes or chronic myelomonocytic leukemia: a propensity score-matched study Mar 2025 Blood Cancer Journal Myelodysplastic Syndromes (MDS)
Oral complement factor D inhibitor danicopan for paroxysmal nocturnal hemoglobinuria Sep 2024 Expert Review of Clinical Pharmacology Paroxysmal Nocturnal Hemoglobinuria (PNH)
One-year outcomes from a phase 3 randomized trial of ravulizumab in adults with paroxysmal nocturnal hemoglobinuria who received prior eculizumab Dec 2020 European Journal of Haematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
One-year efficacy and safety of ravulizumab in adults with paroxysmal nocturnal hemoglobinuria naïve to complement inhibitor therapy: open-label extension of a randomized study Oct 2020 Therapeutic Advances in Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Observation and treatment in DDX41-mutated acute myeloid leukemia and myelodysplastic syndrome Apr 2023 Blood Cancer Myelodysplastic Syndromes (MDS)
Novel therapeutic choices in immune aplastic anemia Sep 2020 F1000Research Aplastic Anemia
Novel targeted C3 inhibitor pegcetacoplan for paroxysmal nocturnal hemoglobinuria Jul 2023 Clinical and Experimental Medicine Paroxysmal Nocturnal Hemoglobinuria (PNH)
Novel Approaches and Future Directions in Myelodysplastic Syndrome Treatment May 2023 The Cancer Journal Myelodysplastic Syndromes (MDS)
Newly revised 2023 MDS response criteria Apr 2023 Blood Myelodysplastic Syndromes (MDS)
New Approvals in Low- and Intermediate-Risk Myelodysplastic Syndromes May 2025 American Society of Clinical Oncology Educational Book Myelodysplastic Syndromes (MDS)