| Family reflections: pediatric aplastic anemia research; a parent perspective |
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Pediatric Research |
Aplastic Anemia, Pediatric |
| Family reflections: George Elliott: a first-person commentary on pediatric aplastic anemia research |
|
Pediatric Research |
Aplastic Anemia |
| Factor B inhibitor iptacopan for the treatment of paroxysmal nocturnal hemoglobinuria |
|
Blood Reviews |
Paroxysmal Nocturnal Hemoglobinuria (PNH) |
| Exploring treatment strategies for paroxysmal nocturnal hemoglobinuria: an overview of registered clinical trials |
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Current Medical Research and Opinion |
Paroxysmal Nocturnal Hemoglobinuria (PNH) |
| Expert consensus on the management of pharmacodynamic breakthrough-hemolysis in treated paroxysmal nocturnal hemoglobinuria |
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Hematology. |
Paroxysmal Nocturnal Hemoglobinuria (PNH) |
| Experience of life quality from patients with aplastic anemia: a descriptive qualitative study |
|
Orphanet Journal of Rare Diseases |
Aplastic Anemia |
| Existing agents, novel agents, or transplantation for high-risk MDS |
|
Hematology. American Society of Hematology. Education Program |
Myelodysplastic Syndromes (MDS) |
| Excellent Outcomes in Feasibility Study of Radiation-Free Conditioning and Transplant in Pediatric Severe Aplastic Anemia. |
|
Transplantation and Cellular Therapy |
Aplastic Anemia |
| Excellent Outcomes in Feasibility Study of Radiation-Free Conditioning and Transplant in Pediatric Severe Aplastic Anemia |
|
Transplant Cell Therapy |
Aplastic Anemia |
| Evolving therapies for lower-risk myelodysplastic syndromes |
|
Annals of Hematology |
Myelodysplastic Syndromes (MDS) |