Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Sort descending Bone Marrow Disease
Efficacy and Safety of Inhibitors of the Proximal Pathway of the Complement System in Paroxysmal Nocturnal Hemoglobinuria: A Meta-analysis of Randomized Controlled Trials American Journal of Therapeutics Paroxysmal Nocturnal Hemoglobinuria (PNH)
Clinical and neurophysiological aspects of peripheral neuropathy in patients with myelodysplastic syndromes British Journal of Haematology Myelodysplastic Syndromes (MDS)
SOHO State of the Art Updates and Next Questions: An Update on Higher Risk Myelodysplastic Syndromes Clinical Lymphoma, Myeloma & Leukemia Myelodysplastic Syndromes (MDS)
Clinical Outcomes and Healthcare Resource Utilization for Patients With Lower-Risk Myelodysplastic Syndromes Treated With Erythropoiesis-Stimulating Agents Clinical Lymphoma, Myeloma & Leukemia Myelodysplastic Syndromes (MDS)
Detection of PNH Clones can Aid in the Distinction of Aplastic Anemia vs Inherited BM Failure Syndromes: A Single Center Experience and Review of the Literature Clinical Lymphoma, Myeloma & Leukemia Aplastic Anemia, Paroxysmal Nocturnal Hemoglobinuria (PNH)
EPYSQLI (SB12; Biosimilar to Reference Eculizumab) in Asian and Non-Asian Patients With Paroxysmal Nocturnal Hemoglobinuria: Subgroup Analysis of a Global Phase III Randomized Controlled Trial EJHaem Paroxysmal Nocturnal Hemoglobinuria (PNH)
Iptacopan for the treatment of paroxysmal nocturnal hemoglobinuria Expert Opinion on Pharmacotherapy Paroxysmal Nocturnal Hemoglobinuria (PNH)
Oral complement factor D inhibitor danicopan for paroxysmal nocturnal hemoglobinuria Expert Review of Clinical Pharmacology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Pegcetacoplan: the first and only C3-targeted therapy for the treatment of adults with paroxysmal nocturnal hemoglobinuria Expert Review of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Safety and efficacy of danicopan in patients with paroxysmal nocturnal hemoglobinuria: a systematic review and meta-analysis Expert Review of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)

Website Feedback

Please use this feedback form to report website issues only. For other issues concerning patients and families, please email help@aamds.org or use the Patient and Family Helpline here.