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Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
Paroxysmal nocturnal hemoglobinuria: Where we stand May 2023 American Journal of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Paroxysmal nocturnal hemoglobinuria: Where are we going May 2023 American Journal of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Real-world experience of pegcetacoplan in paroxysmal nocturnal hemoglobinuria May 2021 American Journal of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Iron overload after complement inhibitor treatment of Paroxysmal Nocturnal Hemoglobinuria Apr 2021 American Journal of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
HLA-haploidentical stem cell transplantation in children with inherited bone marrow failure syndromes: A retrospective analysis on behalf of EBMT severe aplastic Anemia and pediatric diseases working parties Jun 2024 American Journal of Hematology Aplastic Anemia
Efficacy and safety of the C5 inhibitor crovalimab in complement inhibitor-naive patients with PNH (COMMODORE 3): A multicenter, Phase 3, single-arm study Jul 2023 American Journal of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Myelodysplastic Syndromes: 2021 update on Diagnosis, Risk-stratification and Management Aug 2020 American Journal of Hematology Myelodysplastic Syndromes (MDS)
Distinct and convergent consequences of splice factor mutations in myelodysplastic syndromes Nov 2019 American Journal of Hematology Myelodysplastic Syndromes (MDS)
Clinical decision-making and treatment of myelodysplastic syndromes Dec 2023 American Journal of Hematology Myelodysplastic Syndromes (MDS)
Phase 3 randomized COMMODORE 1 trial: Crovalimab versus eculizumab in complement inhibitor-experienced patients with paroxysmal nocturnal hemoglobinuria Jun 2024 American Journal of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)