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Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
Safety and Efficacy of Pegcetacoplan in Adult Patients with Paroxysmal Nocturnal Hemoglobinuria over 48 Weeks: 307 Open-Label Extension Study Apr 2024 Advances in Therapy Paroxysmal Nocturnal Hemoglobinuria (PNH)
Complement Inhibition in Paroxysmal Nocturnal Hemoglobinuria (PNH): A Systematic Review and Expert Opinion from Central Europe on Special Patient Populations Jun 2023 Advances in Therapy Paroxysmal Nocturnal Hemoglobinuria (PNH)
HDAC4 inhibition disrupts TET2 function in high-risk MDS and AML Jul 2020 Aging Acute Myeloid Leukemia (AML), Myelodysplastic Syndromes (MDS)
Calculator-free point-of-care prognostication in myelodysplastic syndromes. Jan 2019 Am J Hematol Myelodysplastic Syndromes (MDS)
Effectiveness of eculizumab in patients with paroxysmal nocturnal hemoglobinuria (PNH) with or without aplastic anemia in the International PNH Registry Jan 2019 Am J Hematol Aplastic Anemia, Paroxysmal Nocturnal Hemoglobinuria (PNH)
How I Diagnose Low-Grade Myelodysplastic Syndromes May 2020 American Journal of clinical Pathology Myelodysplastic Syndromes (MDS)
Real-world experience of pegcetacoplan in paroxysmal nocturnal hemoglobinuria May 2021 American Journal of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Efficacy and safety of the C5 inhibitor crovalimab in complement inhibitor-naive patients with PNH (COMMODORE 3): A multicenter, Phase 3, single-arm study Jul 2023 American Journal of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Alemtuzumab in relapsed immune severe aplastic anemia: Long-term results of a phase II study Jun 2023 American Journal of Hematology Aplastic Anemia
Alemtuzumab in relapsed immune severe aplastic anemia: Long-term results of a phase II study Apr 2023 American Journal of Hematology Aplastic Anemia