Research Articles | Aplastic Anemia and MDS International Foundation (AAMDSIF) Return to top.

Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
Efficacy and Safety of Inhibitors of the Proximal Pathway of the Complement System in Paroxysmal Nocturnal Hemoglobinuria: A Meta-analysis of Randomized Controlled Trials Oct 2024 American Journal of Therapeutics Paroxysmal Nocturnal Hemoglobinuria (PNH)
Clinical and neurophysiological aspects of peripheral neuropathy in patients with myelodysplastic syndromes Nov 2024 British Journal of Haematology Myelodysplastic Syndromes (MDS)
SOHO State of the Art Updates and Next Questions: An Update on Higher Risk Myelodysplastic Syndromes Sep 2024 Clinical Lymphoma, Myeloma & Leukemia Myelodysplastic Syndromes (MDS)
Clinical Outcomes and Healthcare Resource Utilization for Patients With Lower-Risk Myelodysplastic Syndromes Treated With Erythropoiesis-Stimulating Agents Sep 2024 Clinical Lymphoma, Myeloma & Leukemia Myelodysplastic Syndromes (MDS)
Detection of PNH Clones can Aid in the Distinction of Aplastic Anemia vs Inherited BM Failure Syndromes: A Single Center Experience and Review of the Literature Oct 2024 Clinical Lymphoma, Myeloma & Leukemia Aplastic Anemia, Paroxysmal Nocturnal Hemoglobinuria (PNH)
Iptacopan for the treatment of paroxysmal nocturnal hemoglobinuria Oct 2024 Expert Opinion on Pharmacotherapy Paroxysmal Nocturnal Hemoglobinuria (PNH)
Oral complement factor D inhibitor danicopan for paroxysmal nocturnal hemoglobinuria Sep 2024 Expert Review of Clinical Pharmacology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Pegcetacoplan: the first and only C3-targeted therapy for the treatment of adults with paroxysmal nocturnal hemoglobinuria Dec 2024 Expert Review of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Safety and efficacy of danicopan in patients with paroxysmal nocturnal hemoglobinuria: a systematic review and meta-analysis Oct 2024 Expert Review of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Crovalimab in the paroxysmal nocturnal hemoglobinuria treatment landscape Dec 2024 Immunotherapy Paroxysmal Nocturnal Hemoglobinuria (PNH)