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Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
Acquired Aplastic Anemia Therapies: Immunosuppressive Therapy Versus Alternative Donor Hematopoietic Cell Transplantation Jun 2024 Journal of Hematology Aplastic Anemia
Pharmacokinetics, pharmacodynamics, efficacy, and safety of ravulizumab in pediatric paroxysmal nocturnal hemoglobinuria Jun 2024 Blood Advances Paroxysmal Nocturnal Hemoglobinuria (PNH)
Oral Iptacopan in Paroxysmal Nocturnal Hemoglobinuria. Reply Jun 2024 The New England Journal of Medicine Paroxysmal Nocturnal Hemoglobinuria (PNH)
Oral Iptacopan in Paroxysmal Nocturnal Hemoglobinuria Jun 2024 The New England Journal of Medicine Paroxysmal Nocturnal Hemoglobinuria (PNH)
Oral Iptacopan in Paroxysmal Nocturnal Hemoglobinuria Jun 2024 The New England Journal of Medicine Paroxysmal Nocturnal Hemoglobinuria (PNH)
Granulocyte transfusions in severe aplastic anemia Jun 2024 Haematologica Aplastic Anemia
HLA-haploidentical stem cell transplantation in children with inherited bone marrow failure syndromes: A retrospective analysis on behalf of EBMT severe aplastic Anemia and pediatric diseases working parties Jun 2024 American Journal of Hematology Aplastic Anemia
Haploidentical stem cell transplantation (haplo-SCT) represents the main alternative for children with inherited bone marrow failure syndrome (I-BMF) lacking a matched donor. This retrospective study, conducted on behalf of the EBMT SAAWP and PDWP, aims t Jun 2024 American Society of Clinical Oncology Educational Book Myelodysplastic Syndromes (MDS)
Iptacopan and danicopan for paroxysmal nocturnal hemoglobinuria Jun 2024 Journal of Managed Care & Specialty Pharmacy Paroxysmal Nocturnal Hemoglobinuria (PNH)
Complement inhibition in paroxysmal nocturnal hemoglobinuria: From biology to therapy May 2024 International Journal of Laboratory Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)