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Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
The trajectory of prognostication and risk stratification for patients with myelodysplastic syndromes Dec 2023 Blood Myelodysplastic Syndromes (MDS)
PNH and complement gene variants Apr 2023 Blood Paroxysmal Nocturnal Hemoglobinuria (PNH)
T cell dysfunctions in myelodysplastic syndromes Jan 2023 Blood Myelodysplastic Syndromes (MDS)
TP53 mutations in myelodysplastic syndromes and secondary AML confer an immunosuppressive phenotype Jul 2020 Blood Acute Myeloid Leukemia (AML), Myelodysplastic Syndromes (MDS)
Alternative donor BMT with post-transplant cyclophosphamide as initial therapy for acquired severe aplastic anemia Apr 2023 Blood Aplastic Anemia
IPSS-M in myelodysplastic neoplasms arising from aplastic anemia and paroxysmal nocturnal hemoglobinuria Jun 2023 Blood Aplastic Anemia
How I Treat Paroxysmal nocturnal hemoglobinuria Jan 2021 Blood Paroxysmal Nocturnal Hemoglobinuria (PNH)
Cost-effectiveness of iptacopan for paroxysmal nocturnal hemoglobinuria Oct 2024 Blood Paroxysmal Nocturnal Hemoglobinuria (PNH)
Secondary Myelodysplastic Syndrome and Leukemia in Acquired Aplastic Anemia and Paroxysmal Nocturnal Hemoglobinuria May 2020 Blood Aplastic Anemia, Myelodysplastic Syndromes (MDS), Paroxysmal Nocturnal Hemoglobinuria (PNH)
Germline DDX41 mutations define a significant entity within adult MDS/AML patients Sep 2019 Blood Myelodysplastic Syndromes (MDS)