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Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
Choice of conditioning regimens for bone marrow transplantation in severe aplastic anemia Oct 2019 Blood Advances Aplastic Anemia
Determinants of low health-related quality of life in patients with myelodysplastic syndromes: EUMDS Registry study Jun 2023 Blood Advances Myelodysplastic Syndromes (MDS)
Similar outcomes of alemtuzumab-based hematopoietic cell transplantation for SAA patients older or younger than 50 years Oct 2019 Blood Advances Aplastic Anemia
Pegcetacoplan controls hemolysis in complement inhibitor-naive patients with paroxysmal nocturnal hemoglobinuria Jun 2023 Blood Advances Paroxysmal Nocturnal Hemoglobinuria (PNH)
Pharmacokinetics, pharmacodynamics, efficacy, and safety of ravulizumab in pediatric paroxysmal nocturnal hemoglobinuria Jun 2024 Blood Advances Paroxysmal Nocturnal Hemoglobinuria (PNH)
Hemolysis events in the Phase 3 PEGASUS study of pegcetacoplan in patients with paroxysmal nocturnal hemoglobinuria Apr 2024 Blood Advances Paroxysmal Nocturnal Hemoglobinuria (PNH)
DNA methylation identifies genetically and prognostically distinct subtypes of myelodysplastic syndromes Oct 2019 Blood Advances Myelodysplastic Syndromes (MDS)
Statin Use in Myelodysplastic Syndromes Is Associated with a Better Survival and Decreased Progression to Leukemia Apr 2023 Blood Advances Myelodysplastic Syndromes (MDS)
Activity of luspatercept and ESAs combination for treatment of anemia in lower-risk myelodysplastic syndromes Apr 2023 Blood Advances Myelodysplastic Syndromes (MDS)
Guideline-based indicators for adult patients with myelodysplastic syndromes Aug 2020 Blood Advances Myelodysplastic Syndromes (MDS)