Pediatric

Cord Blood Transplant

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Topic(s)
Bone Marrow Transplant
Presenter(s)
Filippo Milano, MD, PhD
During this webinar, Dr. Filippo Milano will discuss cord blood transplant and its role in treating blood cancers and hematological disorders. He will discuss the unique benefits of cord blood as a stem cell source, recent advances in transplantation techniques, and strategies to…

Transplant Associated Thrombotic Microangiopathy (TA-TMA)

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Topic(s)
Acute Myeloid Leukemia (AML)
Aplastic Anemia
Bone Marrow Transplant
Myelodysplastic Syndromes (MDS)
Paroxysmal Nocturnal Hemoglobinuria (PNH)
Pediatric Bone Marrow Failure Diseases
Related Bone Marrow Failure Diseases and Malignancies
Presenter(s)
Sumithira Vasu, MD
During this webinar, Dr. Sumithira Vasu will discuss the diagnosis, treatment, and impact of transplant-associated thrombotic microangiopathy (TA-TMA). After the presentation, there will be a question-and-answer session. Questions can be submitted in advance to help@aamds.org.

Health-Related Quality of Life, AAMDSIF 2026 International Bone Marrow Failure Scientific Symposium

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Presenter(s)
Namrata Chandhok, MD
Thomas LeBlanc, MD, MA
Fabio Efficace, PhD
Alison R. Kavanaugh
Pamela C. Egan, MD
Wil L. Santivasi, MD
The session was recorded at the AAMDSIF 2026 International Bone Marrow Failure Scientific Symposium, Co-Chairs Namrata Chandhok, MD, and Thomas LeBlanc, MD, MA Topics and speakers included: How can we measure quality of life in MDS, to inform interventions? - Fabio Efficace, PhD…

Non-Transplant Therapies for Marrow Failure, AAMDSIF 2026 International Bone Marrow Failure Scientific Symposium

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Presenter(s)
Carlos DeCastro, MD
Phil Scheinberg, MD
Regis Peffault de Latour, MD, PhD
Julian Sevilla, MD, PhD
Kasiani Myers, MD
Suneet Agarwal, MD, PhD
This session was presented at the AAMDSIF 2026 International Bone Marrow Failure Scientific Symposium; Co-Chairs Carlos DeCastro, MD, and Phil Scheinberg, MD, PhD. Session topics included: -Androgens, alemtuzumab, anti-cytokine therapies (anti-IL2R, anti-IFN gamma), daratumumab…

Lisa McReynolds, MD,PhD

Institution
NIH
Primary Disease Area of Focus
Acute Myeloid Leukemia (AML)
Myelodysplastic Syndromes (MDS)
Pediatric
About

Lisa J. McReynolds, M.D., Ph.D., joined the Clinical Genetics Branch (CGB) as a clinical fellow in 2016, was promoted to assistant clinical investigator in 2019 and became a Lasker Clinical Research Scholar in 2024. She earned her M.D. and Ph.D. at Albert Einstein College of Medicine, where she studied Smad signaling in a zebrafish model of hematopoiesis in the laboratory of Todd Evans, Ph.D. (2009). Dr. McReynolds then completed a residency in pediatrics at Morgan Stanley’s Children’s Hospital of New York-Presbyterian Hospital and fellowship through the joint program of Johns Hopkins

David Young, MD, PhD

Institution
NIH
Primary Disease Area of Focus
Aplastic Anemia
Paroxysmal Nocturnal Hemoglobinuria (PNH)
Pediatric
About

Dr. Young is a board-certified Pediatrician and Pediatric Hematologist and Oncologist who studies the genetics, molecular biology, and clinical management and treatment of bone marrow failure syndromes, myeloid malignancies, and other genetic disorders. He oversees clinical trials in aplastic anemia and Diamond-Blackfan anemia while also working with non-human primate models of disease and preclinical development. He also serves as the Medical Director for the RUNX1 Natural History Program of the National Human Genome Research Institute. Dr. Young received a B.Sc. from the University of Notre

Julia T. Warren, MD, PhD

Institution
Children's Hospital of Philadelphia
Physician Status
accepting new patients
Primary Disease Area of Focus
Aplastic Anemia
Paroxysmal Nocturnal Hemoglobinuria (PNH)
Pediatric
About

Julia T. Warren, MD, PhD, joined Children's Hospital of Philadelphia in fall 2022. She is a hematologist with the Division of Hematology and the Pediatric Comprehensive Bone Marrow Failure Program.

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