Paroxysmal Nocturnal Hemoglobinuria (PNH)

Living with PNH: A Patient Panel Discussion

Topic(s)

Join AAMDSIF's Leigh Clark for a panel discussion with two longer-term PNH patients, Marlena Connor and Jessi Hackney. Marlena and Jessi talk about their experiences as patients, what they wish they'd knowns when they were being diagnosed, what resources are important to them and…

We Made It! – Kristy Shares her Perspective in January 2021

Read more about We Made It! – Kristy Shares her Perspective in January 2021

We made it to another treatment day without anyone in our family getting sick! The week leading to treatment day has become pretty worrisome for me. What if someone in our family gets sick with or is exposed to COVID? Josh will not be able to get his infusion within the treatment window and then what? The questions I never thought I'd have to wonder about.

Is blood transfusion safe during the COVID-19 pandemic?

Read more about Is blood transfusion safe during the COVID-19 pandemic?

The rapid spread of the coronavirus disease 2019 (COVID-19) pandemic has challenged healthcare systems to re-organize the management of patients in a short period. The causative pathogen of this pandemic is severe acute respiratory syndrome coronavirus 2 (SARS-CoV-2), one of seven coronaviruses that can be found in humans. It is a rapidly mutating, enveloped, ssRNA, beta-coronavirus. The initial reports published after the pandemic spread showed a transmissibility rate of 2.2 and possibly low values of dispersion.

Severe Aplastic Anemia and PNH Diagnoses Came out of Nowhere - Marianna's Story

Read more about Severe Aplastic Anemia and PNH Diagnoses Came out of Nowhere - Marianna's Story

As a typical community college student, Mariana was busy. Classes, studying, day trips, all were part of her life. Yet during one shower, she dropped to the floor, suddenly dizzy. A few weeks later she would be out of breath, with unusual bruises on her skin.

One-year outcomes from a phase 3 randomized trial of ravulizumab in adults with paroxysmal nocturnal hemoglobinuria who received prior eculizumab

Read more about One-year outcomes from a phase 3 randomized trial of ravulizumab in adults with paroxysmal nocturnal hemoglobinuria who received prior eculizumab

Ravulizumab every 8 weeks showed non-inferiority to

Frequency and perturbations of various peripheral blood cell populations before and after eculizumab treatment in paroxysmal nocturnal hemoglobinuria

Read more about Frequency and perturbations of various peripheral blood cell populations before and after eculizumab treatment in paroxysmal nocturnal hemoglobinuria

While red blood cells (RBCs) and granulocytes have been more studied, platelets and reticulocytes are not commonly used in

Paroxysmal nocturnal hemoglobinuria: role of the complement system, pathogenesis, and pathophysiology

Read more about Paroxysmal nocturnal hemoglobinuria: role of the complement system, pathogenesis, and pathophysiology

The

Paroxysmal nocturnal hemoglobinuria: patient journey and burden of disease

Read more about Paroxysmal nocturnal hemoglobinuria: patient journey and burden of disease

Patients with

Paroxysmal nocturnal hemoglobinuria: current treatments and unmet needs

Read more about Paroxysmal nocturnal hemoglobinuria: current treatments and unmet needs

The current standard of care for

Clinical development of our investigational therapy, pegcetacoplan

Original Publication Date

January 8, 2021

Article Source

External Web Content

Dear members of the PNH community, We are excited to share important updates with you regarding the clinical development of our investigational therapy, pegcetacoplan, for the treatment of paroxysmal nocturnal hemoglobinuria (PNH). Since our last update, we have partnered with…

Subscribe to Paroxysmal Nocturnal Hemoglobinuria (PNH)

NFL Player Teams Up with AAMDSIF

Paroxysmal Nocturnal Hemoglobinuria (PNH)

Living with PNH: A Patient Panel Discussion

We Made It! – Kristy Shares her Perspective in January 2021

Is blood transfusion safe during the COVID-19 pandemic?

Severe Aplastic Anemia and PNH Diagnoses Came out of Nowhere - Marianna's Story

One-year outcomes from a phase 3 randomized trial of ravulizumab in adults with paroxysmal nocturnal hemoglobinuria who received prior eculizumab

Frequency and perturbations of various peripheral blood cell populations before and after eculizumab treatment in paroxysmal nocturnal hemoglobinuria

Paroxysmal nocturnal hemoglobinuria: role of the complement system, pathogenesis, and pathophysiology

Paroxysmal nocturnal hemoglobinuria: patient journey and burden of disease

Paroxysmal nocturnal hemoglobinuria: current treatments and unmet needs

Clinical development of our investigational therapy, pegcetacoplan

Website Feedback