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Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
Molecular Taxonomy of Myelodysplastic Syndromes and its Clinical Implications Jul 2024 Blood Myelodysplastic Syndromes (MDS)
Severe breakthrough hemolysis during compassionate use of Pegcetacoplan in paroxysmal nocturnal hemoglobinuria: managing an emergency Jul 2024 Blood Transfusion Paroxysmal Nocturnal Hemoglobinuria (PNH)
Revisiting Timing and Decision Modeling for Allogeneic Hematopoietic Stem-Cell Transplantation in Myelodysplastic Syndromes Jun 2024 Journal of Clinical Oncology Myelodysplastic Syndromes (MDS)
Phase 3 randomized COMMODORE 1 trial: Crovalimab versus eculizumab in complement inhibitor-experienced patients with paroxysmal nocturnal hemoglobinuria Jun 2024 American Journal of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Phase 3 randomized COMMODORE 2 trial: Crovalimab versus eculizumab in patients with paroxysmal nocturnal hemoglobinuria naive to complement inhibition Jun 2024 American Journal of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Acquired Aplastic Anemia Therapies: Immunosuppressive Therapy Versus Alternative Donor Hematopoietic Cell Transplantation Jun 2024 Journal of Hematology Aplastic Anemia
Pharmacokinetics, pharmacodynamics, efficacy, and safety of ravulizumab in pediatric paroxysmal nocturnal hemoglobinuria Jun 2024 Blood Advances Paroxysmal Nocturnal Hemoglobinuria (PNH)
Oral Iptacopan in Paroxysmal Nocturnal Hemoglobinuria Jun 2024 The New England Journal of Medicine Paroxysmal Nocturnal Hemoglobinuria (PNH)
Oral Iptacopan in Paroxysmal Nocturnal Hemoglobinuria Jun 2024 The New England Journal of Medicine Paroxysmal Nocturnal Hemoglobinuria (PNH)
Oral Iptacopan in Paroxysmal Nocturnal Hemoglobinuria. Reply Jun 2024 The New England Journal of Medicine Paroxysmal Nocturnal Hemoglobinuria (PNH)