Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
The Genomics of Myelodysplastic Syndromes: Origins of Disease Evolution, Biological Pathways, and Prognostic Implications Cells Myelodysplastic Syndromes (MDS)
Venetoclax and hypomethylating agent therapy in high risk myelodysplastic syndromes: a retrospective evaluation of a real-world experience Leukemia & Lymphoma Myelodysplastic Syndromes (MDS)
Myelodysplastic syndromes: 2021 update on diagnosis, risk stratification and management American Journal of Hematology Myelodysplastic Syndromes (MDS)
Paroxysmal nocturnal haemoglobinuria (PNH): novel therapies for an ancient disease British Journal of Haematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Danicopan: an oral complement factor D inhibitor for paroxysmal nocturnal hemoglobinuria Haematologica Paroxysmal Nocturnal Hemoglobinuria (PNH)
Imetelstat Achieves Meaningful and Durable Transfusion Independence in High Transfusion-Burden Patients With Lower-Risk Myelodysplastic Syndromes in a Phase II Study Journal of clinical oncology: official journal of the American Society Clinical Oncology Myelodysplastic Syndromes (MDS)
One-year efficacy and safety of ravulizumab in adults with paroxysmal nocturnal hemoglobinuria naïve to complement inhibitor therapy: open-label extension of a randomized study Therapeutic Advances in Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Silver lining: reduced relapse with chronic GVHD after transplant for MDS Clinical Cancer Research: an official Journal of the American Association of Cancer Research Graft Versus Host Disease (GVHD), Myelodysplastic Syndromes (MDS)
Phase II study of the clinical efficacy and safety of tosedostat in patients with myelodysplastic syndromes (MDS) after failure of hypomethylating agent-based therapy Leukemia & Lymphoma Myelodysplastic Syndromes (MDS)
Iron Chelation in Transfusion-Dependent Patients With Low- to Intermediate-1-Risk Myelodysplastic Syndromes Annals of internal medicine Myelodysplastic Syndromes (MDS)

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